Projektall4treat – Alliance for Treatment in HSP and PLS
Grunddaten
Akronym:
all4treat
Titel:
Alliance for Treatment in HSP and PLS
Laufzeit:
23.12.2015 bis 31.12.2018
Abstract / Kurz- beschreibung:
Development of therapies for HSP and PLS faces a multitude of clinical, regulatory and commercial challenges due to the rarity and genetic heterogeneity of these diseases. We propose to form a multinational Alliance for Treatment in HSP and PLS between leading national HSP/PLS networks with the overarching aim to systematically address these challenges and foster development of new treatments for HSP and PLS.
Specific aims:
1. To establish a global collaborative network (Alliance for Treatment in HSP and PLS) between major national HSP/PLS initiatives, including networks across Canada, Europe, and the US.
2. To create a global HSP/PLS Registry that connects existing registries under one umbrella.
3. To collaborate with patient-driven HSP/PLS foundations and advocacy groups to support establishment of a global HSP/PLS Patient Registry.
4. 4. To create a ‘Trial ready’ infrastructure for HSP and PLS
Specific aims:
1. To establish a global collaborative network (Alliance for Treatment in HSP and PLS) between major national HSP/PLS initiatives, including networks across Canada, Europe, and the US.
2. To create a global HSP/PLS Registry that connects existing registries under one umbrella.
3. To collaborate with patient-driven HSP/PLS foundations and advocacy groups to support establishment of a global HSP/PLS Patient Registry.
4. 4. To create a ‘Trial ready’ infrastructure for HSP and PLS
Schlüsselwörter:
Hereditary Spastic Paraplegia
Primary Lateral Sklerosis
Patient Registry
Natural History Study
Trial Infrastructure
Beteiligte Mitarbeiter/innen
Leiter/innen
Neurologische Universitätsklinik
Kliniken und klinische Institute, Medizinische Fakultät
Kliniken und klinische Institute, Medizinische Fakultät
Lokale Einrichtungen
Abteilung Neurologie mit Schwerpunkt Neurodegenerative Erkrankungen
Neurologische Universitätsklinik
Kliniken und klinische Institute, Medizinische Fakultät
Kliniken und klinische Institute, Medizinische Fakultät
Geldgeber
Sherman, Connecticut, Vereinigte Staaten