Project CFTR 262_263 correct – Targeted gene correction of the c.262_263delTT CFTR Gene defect (liquid spray or powder to…

Basic data

Acronym:
CFTR 262_263 correct
Title:
Targeted gene correction of the c.262_263delTT CFTR Gene defect (liquid spray or powder to inhale and/or intravenous injection)
Duration:
01/02/2016 to 31/01/2019
Abstract / short description:
This work program will provide a novel technological platform for the safe and efficient in vivo gene correction of t Cystic Fibrosis. By developing reagents in humanized models, all vectors will be directly translatable to future clinical trials.

Involved staff

Managers

Faculty of Medicine
University of Tübingen

Local organizational units

Paediatrics Department I and Polyclinic
University Children’s Hospital - Department of Paediatrics
Hospitals and clinical institutes, Faculty of Medicine

Funders

Spielberg, Steiermark, Austria
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