Project all4treat – Alliance for Treatment in HSP and PLS

Basic data

Acronym:
all4treat
Title:
Alliance for Treatment in HSP and PLS
Duration:
23/12/2015 to 31/12/2018
Abstract / short description:
Development of therapies for HSP and PLS faces a multitude of clinical, regulatory and commercial challenges due to the rarity and genetic heterogeneity of these diseases. We propose to form a multinational Alliance for Treatment in HSP and PLS between leading national HSP/PLS networks with the overarching aim to systematically address these challenges and foster development of new treatments for HSP and PLS.
Specific aims:
1. To establish a global collaborative network (Alliance for Treatment in HSP and PLS) between major national HSP/PLS initiatives, including networks across Canada, Europe, and the US.
2. To create a global HSP/PLS Registry that connects existing registries under one umbrella.
3. To collaborate with patient-driven HSP/PLS foundations and advocacy groups to support establishment of a global HSP/PLS Patient Registry.
4. 4. To create a ‘Trial ready’ infrastructure for HSP and PLS
Keywords:
Hereditary Spastic Paraplegia
Primary Lateral Sklerosis
Patient Registry
Natural History Study
Trial Infrastructure

Involved staff

Managers

University Department of Neurology
Hospitals and clinical institutes, Faculty of Medicine

Local organizational units

Department of Neurology with Focus on Neurodegenerative Disorders
University Department of Neurology
Hospitals and clinical institutes, Faculty of Medicine

Funders

Sherman, Connecticut, United States of America
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